c/EPA
           United States
           Environmental Protection
           Agency
            Environmental Monitoring
            Systems Laboratory
            P.O. Box 93478
            Las Vegas NV 89193-3478
EPA/600/4-89/362
November 1989
           Research and Development
Cell Receptor-Xenobiotic
Complexes as Exposure
Biomarkers
           Literature Summary and
           Recommendations

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CELL RECEPTOR-XENOBIOTIC COMPLEXES AS EXPOSURE BIOMARKERS
          LITERATURE SUMMARY and RECOMMENDATIONS
                               by
                          J. A. Santolucito
                    Environmental Research Center
                    University of Nevada-Las Vegas
                    Las Vegas, Nevada 89154-4009
                  Cooperative Agreement No. 814342-01
                      Work Assignment Manager
                         Charles H. Nauman
                 Exposure Assessment Research Division
               Environmental Monitoring Systems Laboratory
                     Las Vegas, Nevada 89193-3478
       ENVIRONMENTAL MONITORING SYSTEMS LABORATORY
             OFFICE OF RESEARCH AND DEVELOPMENT
            U.S. ENVIRONMENTAL PROTECTION AGENCY
                  LAS VEGAS, NEVADA 89193-3478

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                                     NOTICE
      This document is intended for internal Agency use only.







      Mention of trade names or commercial products does  not constitute endorsement or



recommendation for use.
                                        u

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                                     ABSTRACT
       This report presents a brief review of the literature relevant to the interaction between



cell receptor macromolecules and chemicals in their immediate environment. An overview of



the physiological role of cell receptors in relation to endogenous chemical regulators such as



hormones is presented together with the essentials of receptor kinetics.







       While a specific receptor type usually binds only one kind of endogenous chemical, any



number of man-made molecules having the required structural  characteristics (therapeutic



drugs for  example) may also be bound.   Literature is cited demonstrating that certain toxic



environmental chemicals, in addition to drugs, can also bind  to receptor active sites.  Further,



their toxic action is dependent upon the binding.







       The evidence at hand suggests that receptor-bound xenobiotic, rather than total tissue



concentration, may provide a more accurate measure of exposure to environmental chemicals.



However, since most tissues are not readily accessible for  routine monitoring, a surrogate



biomarker of exposure may be developed  using receptor-bound xenobiotics present in the



formed elements of the blood.







       Recommendations are made for research needed to demonstrate the feasibility of blood



cell receptor biomarkers of exposure.
                                           111

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                                     CONTENTS



                                                                                 Page



Notice	  ii



Abstract	  iii



List of Figures and Tables  	  v



Glossary	  vi





Introduction	   1



Cell Receptors-Background	  4



Xenobiotic Modulation of Receptor Numbers/Affinity  	  10



Xenobiotic-Immune System Interaction	23



Research Needs for Development of Receptor Biomarkers	24



Specific Recommendations	31



Literature Cited	35
                                           IV

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                             LIST OF FIGURES



Number                                                               Page



 1	  6



 2	  9










                             LIST OF TABLES






 I 	 11



 H	25



III	26

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       a     Ills:  a
       *c EJE
       EPA/600/4-89/362
       EPA/600/4-89/362
       *b
       EJED
       Santolucito, John A.
1
1






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DELH — | ERR —
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                                                                 19990611
                                                                  Lang:  eng
                                                                  Ctry:  nvu
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Indx:  0
Dates: 1989,
 Desc:
>040
Q088
Q099
^090
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Q245 10 Cell receptor-xenobiotic complexes as exposure biomarkers : *b
literature summary and recommendations / *c by J.A. Santolucito; United States
Environmental Protection Agency. Environmental Monitoring Systems Laboratory.
Q260    Las Vegas, NV :  =t=b Environmental Monitoring Systems Laboratory. Office
of Research and Development. U.S. Environmental Protection Agency, *c 1989.
Q300    47 p. : *b ill.  ; *c 28 cm.
0500    "EPA/600/4-89/362"
      0 Biochemical markers *x Bibliography.
      0 Cell receptors *x Bibliography.
      0 Xenobiotics *x Bibliography.
        Environmental Monitoring Systems Laboratory (Las Vegas, Nev.)
        United States. *b Environmental Protection Agency. *b Office of
Research and Development.

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                                    GLOSSARY

BIOMARKER
       A change in composition or function of a biological system or sample which signals the
occurrence of an event of concern.

CYTOSOL
       The non-membranous cytoplasm bounded by the cell membrane.

DEXTRAN
       A polymer of glucose having both 1-4 and 1-6 linkages, with branches about every five
units, giving it considerable resistance to enzymic hydrolysis.  Molecular weight ranges from
30,000-25,000.

DIOXIN
       A family of planar poh/chlorinated organic compounds consisting of two benzene rings
connected by two oxygen bridges. The congeners differ in their structure and toxicity according
to the number and positioning of chlorine atoms on the molecule.
                                         VI

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ENDOCYTOSIS








       A mechanism whereby cells can internalize molecules aggregated on its outer surface.



An infolding of the membrane results in vesicle formation with envelopment of the aggregated



material.  The vesicle then separates from the boundary membrane,  opens,  and releases its



contents to the cytoplasm.








GLUCOCORTICOIDS



       Steroid hormones,  produced by the  adrenal cortex,  which  regulate  metabolic



interconversions  between carbohydrates, fats and proteins and also exert anti-inflammatory



effects.








HALOGENATED



       The chemical designation of a molecule containing one or more halogen (e.g., chlorine



bromine, etc.) atoms.








IMMUNOGLOBULIN



       Any  of five structurally and antigenically  distinct antibodies produced  by lymphoid



tissue and present in the serum. Specifically, IgA, IgD, IgE, IgG, and IgM








INVAGINATE



       To fold inward, creating a pocket or vesicle.
                                         vu

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LIGAND
       An organic molecule attached to a specific site on  a  macromolecule or membrane
surface.

MICROSOMAL MONOOXEGENASE
       Any of a group of enzymes,  located in microsomes, that catalyze  the  oxidation of
organic compounds.
MONOCLONAL ANTIBODES
       Antibodies derived from one B-lymphocyte cell line.

MUSCARINIC RECEPTOR
       Receptors for acetylcholine located on smooth and cardiac muscle cells in contrast to
those located on skeletal muscle cells, termed nicotinic receptors.

NEUROTRANSMITTER
       Amine or peptide chemicals released by neurons which  result in transmission of nerve
impulses across  synaptic junctions.

OUABAIN
       A gtycoside prepared from Strophanthus gratis.  Acts similar to digitalis on the heart,
resulting in increased strength and regularity of beat.
                                        vui

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PHARMACOKINETICS



       The mathematical description of the fate of drugs in the  body including absorption,



distribution, metabolism, and excretion.








POLYCLONAL ANTIBODIES




       A mixture of antibodies produced by more than one type of B-lymphocyte.







STEREOSPECIFIC



       Three-dimensional organic structures whose molecules have an ordered (crystalline)



orientation rather than the random (amorphous) form.







XENOBIOTIC



       Pertaining to organic substances foreign to the body.

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                          CELL RECEPTOR BIOMARKERS
INTRODUCTION







       Under the Federal Insecticide,  Fungicide, and Rodenticide Act (FIFRA), and other



environmental protection laws, the U.S. Environmental Protection Agency (EPA) is responsible



for  pesticide regulation and  to  ensure  that  unreasonable  risks to human  health or the



environment do not result from exposure to pesticides.  Quantitative health risk assessment



requires that both toxicity and exposure assessments be made (1).  Thus, accurate exposure



assessments become critical to the evaluation of environmental and human health risks  of



pesticides and to the subsequent  development of control regulations that may  be needed for



their protection.







       Assessments may be made of external exposure, i.e., the sum of the xenobiotic material



presented to the absorptive surfaces of an organism, or of internal dose, i.e.,  the amount  of



xenobiotic actually absorbed (2).  Biological markers of internal dose may obviate the need for



estimating the amount of xenobiotic absorbed, which must be done when exposure assessments



are derived from environmental monitoring data.   Indexes of internal  dose range from

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measurements of the tissue/body fluid concentration of a xenobiotic and/or its metabolites, to



the measurement of a biochemical or physiological reaction at the cell, organ, or organism level.







       At the  molecular level,  a  chemical pollutant or its  reactive metabolite binds  to a



receptor protein which may in turn produce a disturbance in intermediary metabolism at the



cellular level.   When the disturbance is of sufficient degree,  a perceptible and measurable



biochemical, physiological, or behavioral dysfunction occurs.   The degree of dysfunction, as



determined by controlled laboratory studies, provides a measure of the toxicity of the chemical.



The close association of xenobiotic-receptor concentration with the metabolic processes leading



to toxicity suggests that  exposure assessments based on the amount of xenobiotic bound to



receptor protein may support more accurate risk  assessments than those based on the  total



amount of xenobiotic present in the organism or one of its tissue compartments.







       In order to prevent unacceptable health risks, the measurement methods used must be



sensitive enough to detect concentrations of receptor-bound xenobiotic below the threshold of



physiological dysfunction. Immunoassays have the required sensitivity (3), and the antigenicity



of receptor protein to which the xenobiotic is bound will facilitate production of the antibodies



needed for  the assay procedure.  Biomarkers that measure exposure (i.e.,  receptor-bound



pesticide) to  the most  sensitive (target)  tissues will have  the greatest relevance to  risk



assessment. However, sampling of that tissue often requires the use of invasive procedures and



are thus nnsuited for routine exposure monitoring of human populations.  Accordingly, this



report will evaluate, through a review of the  literature, the occurrence of and potential for using

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measures of xenobiotic compounds bound to receptor macromolecules in the formed elements



of the blood as surrogate biomarkers of human exposure.  The ease of access of blood samples



compared to other tissues makes them a realistic choice.  Receptors associated with cells or cell



fragments found in other body fluids will also be addressed briefly when appropriate.







       With certain exceptions (e.g., steroid hormones), receptors for hormones, neurotrans-



mitters, and other chemical signals are believed to be located on the cell membrane surface (4).



Cell membrane receptors are an integral part of the plasma membrane structure and serve to



discriminate,  with high specificity  and efficacy,  the  ligand(s) present in  the  immediate



environment surrounding the cell (5).  The high affinity of receptor macromolecules assures



binding of ligand at low concentrations.







       The early conceptual framework for the study of receptor-ligand interaction  evolved



from pharmacologic investigations of drug action during the second half of the  19th century.



Since most drugs bind to receptors designed for interaction with endogenous hormones and



neurotransmitters, these studies also demonstrated receptor mediation of physiologic hormonal



regulation. Xenobiotic-receptor interaction was also suggested in this period with the finding



that lead has a greater affinity for certain tissues, notably those of the central nervous system



(CNS), than for others (6).  Experimental evidence for the binding of xenobiotics to cellular



receptors has  developed relatively rapidly in the past decade.  For example, the Ah receptor,



which  is responsible for the induction of microsomal monooxygenases by polycyclic aromatic



hydrocarbons, has also been found to mediate the toxicity of 2,3,7,8-tetrachlorodibenzo-p-dioxin

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(TCDD) (7).  Also, three major classes of chlorinated hydrocarbon insecticides have been



found to be potent, competitive,  and stereospecific inhibitors of the 7-aminoburyric acid



(GABA) receptor in brain tissue (8).







       The  foregoing  emphasizes the three cornerstones of the rationale for developing



membrane receptor  biomarkers.   First,  the amount  of  xenobiotic  bound  to  cell-receptor



macromolecules at a specific time may afford a physiologically meaningful biomarker of



exposure. This view is supported by the observation that the polybrominated biphenyl (PBB)



concentration of the white blood cell fraction correlates better with  severity of lymphocytic



dysfunction than does the PBB concentration in the plasma fraction (9).  Second, at very low



concentrations xenobiotic-receptor complexes are measurable using immunoassay techniques.



And third, xenobiotic-receptor binding also mediates  a  pollutant-induced adverse effect when



the internal dose becomes sufficiently high.  Therefore, information gained from investigations



of xenobiotic binding to receptor macromolecules may advance the development of exposure-



as well as effects-biomarkers.
CELL RECEPTORS - BACKGROUND







       Receptors have been identified and have been shown to mediate physiologic as well as



pathologic reactions for hormones, neurotransmitters, viruses, bacteria, immunoglobulins, and



chemoattractants (10,11,12,13).  Receptor-ligand interactions are reversible reactions involving

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all the components of the membrane, viz., protein, carbohydrate, and lipid.  Binding sites may



be competitively inhibited by a molecule that resembles the ligand.  They may also be inhibited



non-competitively by molecules that react with sites other than the ligand binding site, causing a



structural change that interferes with the signal transduction function of the  receptor.   The



membrane-receptor macromolecule, composed of an assembly of proteins or glycoproteins, is



embedded in  the  lipid bilayer.    Receptor active sites  are small portions of the molecule



generally making up less than 10% of the total amino acid residues.  They are often clefts in the



surface of the macromolecule, composed mostly of hydrophobic residues but  also containing



polar groups that participate in binding (14).  In glycoprotein receptors, the carbohydrate units



are usually clustered on the periphery of the molecule so that this hydrophilic area is exposed to



the external side of the cell membrane.







       Some  of the  glycoproteins may extend  their contact to the cytoplasmic side of the



membrane, providing a means of internalizing an external chemical stimulus such as a hormone.



The carbohydrate units of glycoproteins are covalentry bonded to the polypeptide  backbone.



Carbohydrate prosthetic  groups can, of course, be part of the ligand molecule as well as of the



receptor macromolecule.  In general, carbohydrate moieties of glycoproteins contribute to the



stabilization of protein conformation and the regulation of metabolic half-life in the circulation



of the intact animal, uptake by cells, message transmission, etc.  (5).  Some  of the receptor



macromolecule features described are represented in Fig. 1.

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                    Outer
                    Protein
                    Layer
                                  Receptor  Macromolecule
                Lipid Bilayer
                        Inner
                        Protein
                        Layer
                                            Channel
                                                                      Receptor
                                                                      Active  Sites
                                                                            o>
                                                                            c
                                                                            (0

                                                                            -Q

                                                                            E
                                                                            
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       In most cells the number of receptors  is under some regulation at the level of gene



expression. Also, many receptor macromolecules contain one or more binding sites for specific



regulatory molecules in addition to the ligand-specific binding site.   Interaction between the



subunits are  of two types:  either  an alteration in the activity of the  regulatory-molecule



binding-site  when ligand binds to the active  site,  or  an alteration in the  activity of the



ligand-binding-site when the regulator site is occupied. The number of cell surface binding sites



is also regulated by cycles of endocytosis, reutilization, and degradation (14).







       From this brief overview, it can be seen that the magnitude of an effect resulting from a



given concentration of hormone,  drug,  or xenobiotic  may vary according to the available



number of cell membrane receptors in existence at the time. Data from a number of systems



suggest that  all the necessary information for activation of the effector is contained  in the



receptor,  i.e.,  some receptors phosphorylate,  others  aggregate, while still  others exist in



multiple-binding  states.  Receptor macromolecules can consist of subunits and can undergo



reversible interactions in the lateral plane of the plasma membrane.   Experimental techniques



allow measuring the physical characteristics of the receptor while  still a  component  of the



membrane or whole cell as well  as  measuring its characteristics in purified  form following



membrane solubilization with suitable detergents (12).







        A receptor is defined or identified, in the  first place, in terms of its pharmacokinetics.



Substances that effectively mimic or block the effects of the principal  ligand should compete for

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binding sites at low concentration. Others should compete only at very high concentrations, if



at all.







       To distinguish receptor-binding (specific) from "other" binding (non-specific) there must



be a finite number of binding sites of rather high affinity, i.e., having dissociation constants in



the nanomolar  range or lower.   This  can  be demonstrated by  adding more and more



radiolabeled compound and noting that binding increases until saturation occurs, i.e., all sites



are occupied. In a binding assay, the membrane component (receptor) is selectively exposed to



a radioactively labeled ligand  to  determine the rate at which  the  ligand  attaches-kj



(association), and is removed--!^ (dissociation), i.e.,



              kj = the rate constant for [L] + [R] => [L.R], and



              kj = the rate constant for [L.R]  => (L] + [R].







  The apparent equilibrium dissociation constant of the receptor, Kd, can then be calculated (=



ICj/lCj) and is usually on the order of 10~9 - 10~12 M.  The Kd represents the concentration of



ligand that results in one-half the total number of receptor sites being occupied at equilibrium.



An increase in Kd correlates with a decrease in affinity.  In addition, the maximum number of



binding sites can be estimated by measuring the quantity of ligand necessary to saturate all the



available binding sites (B^).







       This approach is complicated  by the  fact that radioligands will bind to a variety of



membrane constituents, only one of which represents the receptor of interest. However, this

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non-specific binding can be corrected by measuring the total radioligand bound following its



addition alone, then determining its binding in the presence of excess (usually 100 times the K.



concentration)  unlabeled  ligand  (blank).    The difference (total  - blank)  represents



receptor-specific binding (14).  Binding properties  of receptors are quantitated by Scatchard



plots in which the ratio  of bound-ligand to free-ligand is plotted on the ordinate against bound



ligand  on the abscissa (15).  When a single ligand is interacting with a single population of



receptors possessing a single affinity for the ligand,



              -l/Kd =  the slope of the straight line  obtained,



              Bfflax/Kd  = the y-intercept, and



              Bmax = the x-intercept (Fig. 2).
                              •o
                              a
                                           Slope = -1/K.
                                      [Bound]
B
           Fig. 2.  Illustration of a Scatchard plot showing derivation of Kd and B
                                                                           max

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       However, as pointed out by Rosenthal (16), Bmax must be interpreted as representing



the total number of binding sites rather than the number  of receptor macromolecules, since



each macromolecule may have more than one binding site.  Until the receptor is purified and



its structure known, Bmax is determined in units of fmol/mg membrane protein.







       A number of mammalian cell membrane  receptor systems which bind endogenous



regulatory chemicals have been characterized functionally as well as structurally to varying



degrees (Table I). Purification of some receptors, e.g., insulin receptors, may be hampered  by a



low occurrence or physical similarity to surrounding membrane protein, or both. On the other



hand, the muscarinic cholinergic receptor that binds acetylcholine is relatively more abundant



and easily separated and has been well characterized.







XENOBIOTIC MODULATION OF RECEPTOR NUMBERS/AFFINITY



 Membrane Receptors







       Ah Receptor  The induction receptor for the potycyclic aromatic hydrocarbon-inducible



microsomal monooxygenases,  cytochrome(s) Pa-450, (sometimes designated the TCDD" or



"dioxin" receptor) was identified by Poland et al.(\T).  Later studies revealed that this protein



regulates the expression of a gene battery which includes the structural genes for cytochrome(s)



Pj-450 and in certain tissues, in concert with at least one other regulatory locus, alters patterns



of cell proliferation and differentiation.  For a review of these developments, see Poland and



Knutson (18).
                                          10

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TABLE I. Verified hormone/transmitter receptor systems
Designation
^-adrenergic
dp a2-adrenergic
Acetyl Choline
Insulin
Glucocorticoid
Estrogen
Thyroxine
Growth Hormone
Vasopressin/
Oxytocin
Substance P
Endorphins
Histamine
GABA
Dopamine
Ligand(s)1
E,NE
E,NE
Ach
Insulin
Cortisol
Estradiol
T3
Somatotrophin
Vasopressin/
Oxytocin
Substance P
^-Endorphins
Histamine
TT-Aminobutyric acid
Dopamine
CeU
Location2
PM
PM
PM
PM
C;N
C;N
PM,C,M,N
PM
PM
PM
PM
PM
PM
PM
Occurrence3
wbc;s;sk;c;hp;ns
hp;s;sk;c;wbc;ns
wbc;ns;s;sk;c
wbc;wd
wbc;wd
ut, wd
wbc;wd
wbc;wd
wbc;ns;sm
wbc
wbc
wbc
ns
ns
Ref.
(11,13)
(11,13)
(10,13)
(11)
(13)
(20)
(10,13)
(12,13)
(13,21)
(13)
(13)
(13)
(12)
(13)
1 E = epinephrine; NE^norepinephrine; Ach=Acetylcholine; T3=triidothyronine.
2 PM=plasma membrane; N»nucleus; C=cytosol
3 s=smooth muade; sk=skeletal muscle; c=cardiac muscle; hp=liver; ut = uterus; pi=platelet;
  rbc=erythrocyte; wbc=leukocyte; ns=nervous system; pnc=pancreas; wd=widely distributed.
                                         11

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       The administration of 3-methylcholanthrene (MC) and structurally related polycyclic



aromatic hydrocarbons (PAH) results in the induction of cytochrome P1-450 and associated



monooxygenase activities, including aryl hydrocarbon hydroxylase (AHH) in some but not all



strains of mice (19).  PAH responsiveness in some strains of mice is inherited as a simple



autosomal dominant trait.  The gene locus controlling this trait was designated  the Ah locus.



Available data indicate  that the  receptor  protein  for 2,3,7,8-tetrachlorodibenzo-p-dioxin



(TCDD), MC, and other inducers is the product of the Ah locus (17). Studies to determine the



subcellular distribution of the Ah receptor in mouse hepatic tissue suggest a cytosolic as well as



a nuclear compartment.   Comparisons have been made between species of the relative



concentrations of Ah receptor in hepatic and extrahepatic tissues.  Interspecies differences exist



with respect to the tissue distribution of the Ah receptor as well as the relative concentrations



of this protein in those tissues possessing the protein (19).







       The direct  demonstration of the occurrence of a receptor  protein for TCDD in human



lymphocytes (22) and human squamous cell carcinoma lines (23) has been reported.  Binding



studies using [3H]TCDD demonstrated the presence of the Ah receptor in the cytosolic fraction



from cultures of human  squamous cell  carcinoma of epidermal origin  (17).   The relative



amount  of receptor measured in different cell lines correlated  with  the maximally induced



activity of the monooxygenase 7-ethoxycoumarin O-deethylase (ECOD)(23).  Studies using cell



cultures of cortical thymocytes (T-lymphocyte precursors) and medullary thymic epithelial cells



treated with TCDD have suggested impaired differentiation of intrathymic precursor cells for
                                           12

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the observed TCDD-induced thymic atrophy seen in the intact animal (24). The potential for a



direct effect of TCDD on cultured human lymphocytes has not been as extensively explored.







       An  excellent correlation was  demonstrated between the binding affinities  of  23



halogenated dibenzo-p-dioxin and dibenzofuran congeners in vitro,  and a measure of their



potencies in vivo (25). The charcoal-dextran binding assays were performed using rat hepatic



cytosol receptor protein.  At a given concentration, the amount of receptor-chemical complex



formed is proportional to the affinity constant of the ligand. Potencies (ED^) to induce AAH



activity were determined in the intact rat.







       Thus, the amount of receptor-chemical complex may provide a more physiologically



meaningful measure of exposure to TCDD and  related compounds than would total tissue



concentration.   Further,  the ease  of acquiring a blood sample for  measuring complexed



lymphocyte Ah receptor would facilitate routine monitoring of human exposures to these



chemicals.







       Gamma aminobutvric acid Receptor Neurotransmitters (neurohormones) are chemical



signals used by nerve cells to communicate with each other and with muscle or gland cells. They



are amino acids or small  potypeptides released by one cell and  received  by another  via



stereospecific receptor sites. Binding of the neurotransmitter to its receptor causes a change in



receptor conformation and initiates a change in membrane potential
                                          13

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       Neurons in the brain utilize a number of neurotransmitters in addition to the familiar



acetylcholine and norepinephrine found in peripheral nerves.   One of these, ir-aminobutyric



acid (GABA), and its receptor complex have received considerable attention in recent years.



The receptor model which has emerged is that of a protein having at least three interacting



components:  one that binds GABA, another that binds benzodiazepine (BZ) tranquilizers, and



another which binds the convulsants picrotoxinin (PTX) and bicyclophosphates (26). These sites



interact allosterically and affect each other's binding through conformational changes (27,  28).



Activation of most GABA receptors (GABAR) in mammals leads to an influx of Cl" causing



membrane hyperpolarization (29).







       The ligand of choice for studying agonists and antagonists of the PTX binding site



within the GABAR complex is t-Butylbicyclophosphorothionate (TBPS) (30). It was selected



because of its specificity (no more than 33% non-specific binding), high affinity (Kd = Ca  17 x



10"9 M), and because t-butylbicyclophosphite is easily labeled with ^S in a single step to form



[^SjTBPS.   The relatively high specific activity (about  30 Ci/mmole at the start),  and the



relatively short  half-life of ^S (about 90 days), permit a fresh batch of pSITBPS to be used for



about 6 months. Its binding and displacement properties  remained constant over this period.







       Most insecticides are neurotoxins that inhibit acerylcholinesterase at synapses or disturb



sodium channels on nerve or muscle cell membrane. Some, however,  exert their primary toxic



action on the GABAR found in the vertebrate and invertebrate central nervous systems as well



as in invertebrate neuromuscuiar junctions.  Included are certain cyclodiene (e.g., dieldrin) and
                                          14

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hexachlorocyclohexane  (e.g.,  lindane) insecticides  (29),  and three of the components of



toxaphene, which probably account for most of the toxicity of the commercial product which has



at least 188 components (31). These insecticides inhibit GABA-induced chloride permeability



and may account for their stimulant and convulsant effects.  On the other hand, competitive



binding  studies with some of the potent  cr-cyano-3-phenoxybenzyl pyrethroid insecticides



suggest that they bind to a site closely associated with, but possibly distinct from, that of TBPS



and PTX (32).







        The density of specific [^SJTBPS binding sites varies in different regions of the brain,



being highest in cerebral cortex (Ca. 65 pmoles/g) and lowest in  the pons-medulla (Ca. 14



pmoles/g) (30). Relatively few studies report a systematic search for the presence of GABAR



in non-nerve tissues.  Squires (30) found specific TBPS binding in rat liver and lung tissue to be



about 7% and 2%, respectively, of that seen in cerebral cortex, while no specific binding was



demonstrated in kidney tissue. [3H]-muscimol, a potent GABA agonist used to label GABAR



sites in vertebrate brain, was found to bind specifically to sites in a crude membrane fraction



prepared from bovine  cerebral blood vessels (33).  GABA receptors have been reported in



guinea pig ileum and vas deferens (34).







       The BZ receptor in brain tissue occurs in a macromolecular complex that includes a



binding site for the inhibitory neurotransmitter GABA.   While most BZ binding sites are



associated with GABA receptors, a few studies have demonstrated the existence of one without



the other in some rat brain preparations (35). The  GABA-BZ receptor complex also includes
                                          15

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recognition  sites for  barbiturates and possibly  ethanol.   In initial studies of 3H-diazepam



binding,  peripheral tissues were examined  as controls (36).  Surprisingly, high densities of



diazepam binding sites were observed in a variety of peripheral tissues with similar nanomolar



affinity for diazepam as the central receptors.  High densities of these receptors have been



found in rat adrenal cortex (but not medulla), salivary glands, testes, and ovaries.  Pancreas and



pituitary tissue have  relatively low densities of receptors.  The  physiological significance of



these peripheral BZ receptors is unclear.







       Nevertheless, the association of BZ and GABAR sites in central nervous system tissues



and the occurrence of diazepam receptor sites in peripheral tissues give reason to investigate



the possible occurrence  of receptors for  pesticides (e.g., dieldrin, lindane, toxaphene,  and



cypermethrin) in blood cell membranes.







       Acetylcholine  Receptor   The acetylcholine receptor (AchR) is a well-characterized



component of synaptic and neuromuscular transduction systems.  This receptor  translates the



binding of the neurotransmitter acetylcholine (Ach) into a rapid increase, then decrease, in the



permeability of the membrane to the passage of cations (Na*, K*). AchR sites are sub-units of



a macromolecular receptor complex containing other agonist and/or antagonist binding sites.



The enzyme acetylcholinesterase (AchE) and the AchR either occupy neighboring sites on the



same macromolecule or sites on separate molecules that are coupled in such a way as to permit



coordination of function (37). AchE is an extrinsic protein (i.e.,  it is readily dissociated from
                                           16

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membrane preparations of vertebrate muscle endplate),  while AchR is an intrinsic protein



embedded within the membrane structure (38).







       The  presence  of AchE on  erythrocyte membranes  is well documented,   and the



inhibition of this enzyme's activity is used to assess exposure to organophosphate insecticides



(39).  The AchR has  been reported in rat lymphocyte membranes (13).  Whether the close



association of AchR and AchE seen in neural and muscular tissue also holds for RBC and/or



WBC membranes has not been reported.







       There is evidence for interaction of organophosphate insecticides with RBC membrane



protein other than AchE.  Erythrocytes from humans exposed to organophosphate insecticides



were  found  to have altered membrane stability (40).  Human subjects with serum or blood



AchE inhibition between 40-60% were considered mildly intoxicated, and those with more than



60%  inhibition as  severely intoxicated.   Erythrocyte membranes from mildly intoxicated



subjects were more  resistant, while those from severely intoxicated subjects were less resistant



to hypotonic hemotysis. Also, a significant increase in membrane phosphatidylcholine was seen



in the severely intoxicated.  This suggests a binding of organophosphate to RBC membrane



macromolecules.  Whether this binding involves the AchR receptor and/or can be utilized as a



biomarker of exposure is unknown.







       Dnpaming Receptor The dopamine-sensitive site in the brain and pituitary to which



neuroleptics bind with high affinity has been studied  intensively  in  the  search for new
                                          17

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therapeutic agents. Its functional molecular size is known, though it has not been characterized
structurally.  There appear to be multiple receptors for dopamine, some linked to the adenylate
cyclase and others not (13).

       The ligand spiroperidol binds specifically to dopamine receptors and is commonly used
to study dopamine receptor agonists and antagonists.  The specific binding of this ligand in
membrane preparations from brain cortical tissue was found to be inhibited in the presence of
lead and mercury (41).   Tri-n-butyl lead was a more potent inhibitor than lead acetate, and
mercurous chloride was more potent than methylmercuric chloride. Although the specificity of
the heavy  metal binding to receptor protein was not reported, clearly the affinity of the receptor
site for dopamine was altered.  The blocking action was not  indiscriminate, since the heavy
metals were relatively ineffective in blocking giycine, GABA, or diazepam receptors. However,
they did inhibit the binding of 3H-quinuclidinyl benzilate (^-QNB), a specific ligand for the
muscarinic AchR.

       Adrenergic Receptor  Adrenergic receptors (adrenoceptors) have high specificity for
the catecholamine neurotransmitters epinephrine  and norepinephrine.   While they  are
abundant  in nerve and smooth muscle tissues,  they can be found in most human tissues
including erythrocytes and lymphocytes (42).  ^-receptor concentration increases from late fetal
life to adulthood; in most tissues and decreases with age thereafter. As rat reticulocytes mature
to erythrocytes, the 0-adrenergic receptors decrease by ca. 66%.
                                          18

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       Four main receptor sub-types are recognized.  The ^- and 02-adrenergic receptors



stimulate the membrane-bound enzyme, adenylyl cyclase, thus raising intracellular cyclic AMP



levels.  The or2-adrenergic receptors inhibit this enzyme, whereas the or.-adrenergic receptor



leads to the hydrolysis of polyphosphoinositides which,   in  turn, generates two  secondary



messengers, inositoltriphosphate and diacylglycerol (43).







       Methyl mercury exposure to mice in utero produced a dose-dependent increase in the



adrenergic receptor binding in liver and kidney tissue which  persisted throughout the first 5



weeks of postnatal life.   The animals' physiological reactivity to adrenergic stimulation was



altered in a manner consistent with the increased receptor binding capacity (44).  The  authors



suggest that methyl-mercury exposure in utero  alters adrenergic responses  through targeted



effects on post-synaptic receptor populations in specific tissues.  Modulation of ^-adrenergic



receptor activity by cardiac glycosides has also been reported. A single neonatal treatment with



either ouabain or digoxin resulted in increased  responsiveness to adrenergic  excitation of



two-month-old adult rats (45).







       Additional work would be required to determine first,  whether the receptor population



increase would persist with continued exposure,  and second, whether the  phenomenon has



potential as a biomarker of in utero and/or postnatal exposure. However, the results reported



(44,  45) verify the link between receptor population  and potential for response and lends



further support for evaluating receptor-bound xenobiotic concentration as the physiologically



meaningful measure of exposure.
                                            19

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Cytosolic/Nuciear Receptors







       Receptors for some steroid hormones have been identified in target tissue cytosolic-



and/or  nuclear-fractions  as  well  as in cell  membrane-fractions.    Receptors  which are



membrane-bound interact primarily with neighboring macromolecules, while the soluble and



more mobile cytosolic receptors can interact with a greater variety of systems within the



cytoplasm,   including nuclear DNA.    A review  of  the experimental data  suggests the



membrane-mediated effect of the  hormone is probably different from the cytosolic/nuclear



receptor-mediated effect (46).   For example,  the cytosolic/nuclear receptor for a steroid



hormone may mediate a protein anabolic response, while the membrane-bound version of the



same receptor may mediate an increase in intracellular cyclic AMP.







       Receptors for most non-steroidal hormones/neurotransmitters are found only in the



plasma membrane.   One exception is the receptor for thyroxine, (T3), which occurs as both



membrane-bound and cytosolic (10), a finding which is consistent with the many intracellular



effects induced by T3.







       Estrogen Receptor The  receptor macromolecule for estrogen is found in a number of



tissues including pituitary glands, gonads, smooth muscle of the reproductive tract, brain, etc.,



reflecting the rather widespread actions of estrogenic hormones.
                                          20

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       An anti-estrogenic effect on rat pituitary cell cultures was reported for the pesticide



chlordecone (Kepone) (47).   Pretreatment of pituitary gonadotrophs with estradiol-170 (E,)



alone enhanced their response to gonadotrophin-releasing hormone (GnRH) in tissue culture.



This response could be  inhibited by pretreatment with E2 plus Kepone.   The  approximate



two-fold increase in secretion of follicle stimulating hormone (FSH)  and luteinizing hormone



(LH) caused by E2 pretreatment was depressed by Kepone in a dose-dependent manner.  A



related pesticide, Mirex, did not suppress the GnRH response at any concentration.  It was



noted that Kepone had little or no effect on basal FSH and LH secretion.







       An estrogenic action has been reported for several pesticides which appear to bind to



estrogen receptor macromolecules. Among these are o,p'-DDT and/or o,p'-DDE, Kepone, and



the mono- and bis-phenol metabolites of Methoxychlor  (48).   The apparent  disagreement



concerning the effect of Kepone (47 vs. 48) may result from its ability to competitively inhibit



E2 in the in vitro test system, while expressing an inherent weak estrogenic activity in an in vivo



test system lacking other sources of estrogen.







       A rather extensive literature confirms the estrogenic activity exhibited by a number of



pesticidal compounds  or their  metabolites,   as evidenced by  their ability  to  stimulate



reproductive tract tissues in vitro and in vivo. On the other hand, demonstration of estrogenic



effects on the CNS and/or behavior have been less consistent. For example, administration of



these compounds to neonatal animals fails to influence sex differentiation. However, a recent



report  clearly shows a CNS/behavtoral effect of methoxy-chlor when  administered to
                                          21

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ovariectomized female  rats and hamsters (49).   These animals  exhibited increased  acyclic



running wheel activity as well as persistent vaginal estrus, and displayed reproductive behaviors



following progesterone administration.







       While recent studies have demonstrated that TCDD significantly reduces uterine and



liver estrogen receptor levels in rats (50), earlier studies had shown that several other inducers



of the mixed function oxidase system decreased estrogen binding in rat liver preparations (51).



Whether these compounds compete for the estrogen receptor or in some way alter its  affinity



was not determined.







       Glucocorticoid Receptor Glucocorticoid receptors (GRc) are found in most tissues,  an



observation consistent  with  the regulatory action of the  glucocorticoid  hormones on fat,



carbohydrate, and protein metabolism. GRc are also present in lymphocytes (Table I).







       The maximal binding capacity (BMX) of skeletal muscle cytosolic GRc was reduced in



rats treated with  TCDD (52).  A similar reduction of hepatic cytosolic GRc binding capacity



was  effected  in  pregnant mice treated  with either 2,3,4,7,8-pentachlorodibenzofuran  or



1,2,3,4,7,8-hexachlorodibenzofuran (53).    Interestingly,  these polychlorinated dibenzofurans



also  decreased the binding capacity of hepatic plasma membrane  epidermal growth factor



(EGF) receptors.  Since both  the GRc and  EGF receptor systems have roles in controlling



normal growth and differentiation, they are receiving considerable  attention with respect to



their possible involvement in xenobiotic-induced teratogenesis.
                                           22

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XENOBIOTIC-IMMUNE SYSTEM INTERACTION







       Depressed antibody (B-lymphocyte)  and/or  cell-mediated  (T-lymphocyte) immunity,



indicative of impaired immunocompetence,  occur after exposure to small but not essentially



toxic amounts of certain environmental pollutant chemicals (9).  Included are representatives



from various chemical types. For example:







 Halogenated aromatic compounds-2.3.7.8-tetrachlorodibenzo-p-dioxin. polybromo-biphenyls,



       polychloro-biphenyls, and hexachlorobenzene,



 Heavy metals-cadmium, cobalt, chromium, nickel, and lead,



 Organometallics-methylmercuric chloride, and



 Pesticides-Carbaryl Carbofuran, DDT, Dieldrin, and Methyl Parathion.







       The examples of immune system suppression presented in Table n were excerpted from



a recent review of the subject (9) and are representative of the kinds of responses which have



been observed.  Additionally, the route and timing of the xenobiotic exposure appear  to



influence the immune response.  For example, a single  dose of Cd augmented the antibody



response to an antigen if injected intraperitonealy and diminished  the  response  when



administered orally.   Also, injection  of Cd  14 days before the administration of antigen



increased antibody synthesis, while injection 7 days before decreased it.
                                          23

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       Despite  the considerable  attention given  to immunosuppressive  effects  of



environmental chemicals in recent years, relatively little is known concerning their mechanisms



of action.  While a discussion of the relevant research is beyond the scope of the present report,



it is noteworthy that immunotoxicity by TCDD and PCBs is associated with stereospecific



binding to the Ah receptor present in lymphoid tissue and cells (54).







RESEARCH NEEDS FOR DEVELOPMENT OF RECEPTOR BIOMARKERS.







       A number of receptor systems that have been identified in various tissue types also are



found in the formed elements  of the blood.  Much of the investigative effort concerning



hormone receptors in blood cells originally focused on leukocytes and concerned  interactions



between the neuroendocrine and immune systems.  Examples of these interactions  include



stress-induced  immunosuppression mediated by epinephrine and glucocorticoids,  and



modulation  of  the  neuroendocrine system  by  neuroactive peptides that  are released  by



leukocytes responding to foreign stimuli (13).







       In recent years,  studies have extended to other formed elements in the blood.  A



serious, though not exhaustive,  search  of the literature revealed a respectable number of



receptor systems that have been identified in  blood cells (Table HI).  Clearly, the  information



base exists to warrant a  systematic search for blood cell receptor systems that bind pesticidal



and other toxic chemicals that have high Agency priority.  Complexes thus identified can then



be further evaluated for their potential use as biomarkers of exposure.
                                          24

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                 TABLE n. Xenobiotic Alteration Of Immunocompetence
Chemical1                 Response

Pb            Incr. susceptibility of mice to Salmonella typhimurium.
Pb            Incr. susceptibility of mice to Encephalomyocarditis virus.
Pb            Incr. susceptibility of mice to Langat virus.
Cd            Incr. susceptibility of rats to inoculation with bacterial endotoxin.
Cd            Enhanced mortality of mice inoculated with Encephalomyocarditis virus.
Cd            Enhanced mortality of mice naturally infected with Hexamitis muris.
Hg.,          Enhanced mortality of mice inoculated with Encephalomyocarditis virus. .
Pb.Cd.Hgj .    Lowered antibody response in mice to infectious agents.
Pb,  Cd        Reduced I G antibody synthesis in rodents.
Hj^          Suppressed both primary I M and secondary I G responses.
Heavy metals  Evidence of direct effect on B-lymphocytes to suppress humoral response.
PCB, HCB    Lowered rodent antibody synthesis to sheep RBC (antigen).
HCB         Suppressed cell-mediated and enhanced humoral immunity in rodents.
PBB          Decreased population of T-lymphocytes.
PBB          Better correlation of Lymphocyte dysfunction with PBB concentration in WBC
              fraction than in plasma fraction.
Dioxin        Progeny of mice exposed perinataily showed thymic atrophy.


1- Pb = lead ;Cd = cadmium; Hgj . = inorganic/organic mercury; HCB = hexachlorobenzene;
  PCB=polychlorinated bipheiiyls; PBB=poh/brominated biphenyls.
       An early step in the evaluation of a candidate complex requires in vitro as well as in vivo

studies which will:  (1) compare the affinity constants, for a given xenobiotic, between receptors

recovered from blood cells and  those recovered from  target tissue cells; (2) verify that the

amount of receptor-bound xenobiotic in a blood sample  is potentially detectable;  and (3)

determine the pharmacokinetics of the complex under different  exposure scenarios in vivo, and

the stability of the complex in vitro following withdrawal of the blood sample.
                                          25

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                                     TABLE m
                Receptor Systems Found In the Formed Elements of Blood
                              As Well As in Other Tissues
             Receptor                   Location1                   Ref.


       ACTH                    (m)Leukocyte                     (13)
       Acetylcholine              (m)Leukocyte                     (13)
       a-Adrenergic              (m)Leukocyte, Platelet             (13,11)
       ^-Adrenergic              (m)Leukocyte, platelet             (13,55)
       Ah                        (c)Leukocyte                      (22)
       Endorphin                 (m)Leukocyte                     (13)
       Enkephalin                (m)Leukocyte                     (13)
       Dopamine                 (m)Leukocyte, Pituitary Cells        (56,57)
       Glucocorticoid             (m)Leukocyte                     (13)
       Growth Hormone          (m)Leukocyte                     (13)
       Histamine                 (m)Leukocyte                     (13)
       Insulin                    (m)Leukocyte, erythrocyte          (13,58)
       Interferon                 (m)Leukocyte                     (12)
       Parathyroid                (c)Leukocyte                      (13)
       Prolactin                  (m)Leukocyte                     (13)
       Prostaglandin E1&2          (m)Leukocyte, Erythrocyte          (59, 60)
       Serotonin                  (m)Leukocyte, Platelets            (13,61)
       Somatomedin              (m)Leukocyte, Erythrocyte          (12)
       Somatostatin              (m)Leukocyte                     (13)
       Substance?                (m)Leukocyte                     (13)
       Thyroxine                 (c)Leukocyte                      (13)
       Vasopressin                (m)Leukocyte                     (13)


1. (c) - receptor occurs in cytosolic and/or nuclear fraction
 (m) = receptor occurs in membrane fraction.


       Regarding the comparison of blood-borne and target  tissue receptors, the literature

suggests that the same receptor system obtained from different tissues possess similar in vitro

binding properties. Total binding capacity, reflective of receptor numbers rather than receptor

binding kinetics, are the most frequently reported differences.  Examples include:  the AcR
                                         26

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(62); estrogen receptor (63); the Ah receptor (64); benzodiazepine receptors (36); adrenergic



receptors  (42); and  insulin receptors (65).   Insulin receptors from different human tissues



appear to possess structural as well as functional similarity (66).
       It  is worth noting that interspecies  similarities in  functional and/or structural



characteristics of GABA (35, 67), Ah (19), GnRH (68),  and corticosteroid receptor systems



(69) have also been reported.







       Potential for detectability of the complex cannot be addressed directly because data on



numbers of xenobiotic binding sites per blood cell are lacking.  However, a calculation based on



reported  numbers of insulin  receptors per  erythrocyte  suggests  the feasibility of an



immunoassay on a one milliliter blood sample.  The abundance of insulin receptors per human



erythrocyte has  been estimated  from 6.3-9.9 per RBC (70), up to  >400 binding sites per



erythrocyte (71).  For purposes of illustration,  taking the lower mean value of 8 sites per



erythrocyte  and 4xl06  RBC/mm3  of  blood,   a one  ml sample of blood  contains  4xl09



erythrocytes and 3.2xl010 receptor sites. Dividing by 6 x ICr^approx. Avogadro's number) gives



about 5xlO'14moles of binding potential,  assuming one molecule of ligand per receptor site.



Using the higher value for RBC insulin receptors,  provides about 2xlO"12  moles of ligand



binding potential per ml of blood  Enzyme-linked immunosorbent assays using monoclonal



antibodies are capable of detecting femtomole (10*15 moles) quantities of benzo[a]pyrene-DNA



adduct (72).  The numbers of hormone  receptor sites reported  for leukocytes are generally



greater  than those for erythrocyte insulin  receptors, as can be seen  from the following
                                          27

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examples: 2,000-7,000 0-adrenergic sites/cell, 200or-adrenergic sites/cell, 300 T3 sites/cell, 4,000



growth hormone sites/cell, 7,000 substance P sites/cell,  and 3,000 ACTH sites/cell (13), and



240 prostaglandin E2 sites/cell (60). A similar calculation using 3,000 receptors per leukocyte



and 7,000 WBC per mm3 would provide for 3xlO"12 moles of ligand binding. Thus, the potential



for immunoassays of receptor-bound xenobiotic in the blood does appear to exist.  Further,



should a receptor type occur on both  leukocytes and erythrocytes  and have similar binding



kinetics, an immunoassay screen could be performed on the total cell population of the sample.







       Finally, the kinetics of ligand-receptor interaction which  includes the association (k^)



and dissociation (k,) rate constants,  and the apparent equilibrium  dissociation constant,  Kd,



(kj/lCj) of the receptor can be readily determined (5).  For exposure biomarker use, the Kd of



the complex must be indicative of specific binding. Also important is the rate of dissociation of



the Ligand-receptor  complex.   The  temperature of separation of bound from free ligand



determines the loss of complex in the interval from removing the complex from its equilibrium



melieu to its separation from the mixture (73).  Thus, complexes that dissociate rapidly require



separation techniques that minimize dissociation (assumes that separation began while binding



reaction was at steady state.   Since free ligand is infinitely diluted in the procedure prior to



separation for all practical purposes, reassociation does not occur.







       The  loss  of  binding  due to dissociation  has been  shown to increase approximately



linearly through the first half-life (t1/2) of dissociation of ligand-receptor complexes that follow



first-order kinetics (73). When percent binding loss is plotted on the y-axis against separation
                                           28

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time (in dissociation half-life units) on the x-axis,  it  is seen that a separation procedure



completed in less than approximately 0.15 t: ,2 avoids losing more than 10% of bound ligand.
       Since



                     Kd * [L][R]/[LR]
an  association rate constant,  (1^),  of  106  M'1 sec'1  (a value  frequently obtained  for



neurotransmitter receptors) can be used to show that a ligand-receptor complex having a K . =



10"8 M permits a separation time of about 10 sec., i.e.,







                     10-8 M = 0.693/t1/2/106 M'1 sec'1



       and



                     t1/2 = 69.3 sec. and 0.15t1/2 = 10 sec. (66).







       Continuing the calculations, Yamamura (73) shows:  for Kd = 10"7M, separation must



be complete within 0.10 sec; for Kd - 10"9, 1.7 rain; for Kd • 10'10,  17 min; and for Kd = HT11,



2.9 hr.  For the lower affinity constants, and  depending on the separation time, it may be



necessary to accommodate and correct for higher percentage losses.







       Assessment of an exposure rate from the concentration of receptor-bound xenobiotic in



the blood requires an  understanding of the pharmacokinetics of receptor macromolecules in
                                           29

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vivo.    This  information  is  available  for many  receptor-bound therapeutic  drugs,



neurotransmitters, and hormones, but not for receptor-bound environmental chemicals.







       Important phannacokinetic parameters  of receptor-bound  chemical  following acute



exposure,  assuming first order  kinetics, include the rise-time and  biological half-life of the



receptor-xenobiotic complex in vivo for each exposure route of concern. These values must be



estimated  either from laboratory animal experiments,  and then extrapolated to humans,  or



determined  from successive measurements made on  humans following  a single accidental



exposure.







       Interpretation of receptor-bound  xenobiotic levels resulting from chronic exposure



requires, in addition, information on the total number of receptors present. The phenomenon



of internalization of extracellular material has been described in  which occupied receptor



macromolecules migrate laterally,  aggregate, invaginate,  and enter the cytoplasm within



vesicles.  Endocytosis of receptors may be followed by return of the receptors to the surface



unchanged or by receptor degradation and replacement (74). It is hypothesized that receptor



numbers could remain unchanged,  be decreased if replacement lagged internalization, or be



increased if replacement was overcompensated. Thus, the total number of receptors in exposed



individuals,  compared to those found in non-exposed individuals,  may  help to  establish a



chronic exposure scenario.

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       Finally,  the existence of body fluids,  other than blood, containing cells and/or cell



fragments should be acknowledged. The presence of renal tubular epithelial cells in urine and



spermatozoa in semen may provide a source of receptor macromolecules either not found in



blood,  or found in greater numbers.  Some of the evidence in support of exposure biomarker



development using these fluids was presented in an earlier report (75).







SPECIFIC RECOMMENDATIONS







       A  study to evaluate the potential use of pesticide-receptor complex levels in human



blood samples as  biomarkers of exposure is timely  for several reasons.   Foremost is the



Agency's recognition of the need for rapid, cost-effective screening tests as expressed in the



research strategy for the 1990s (76).  Further, the separate technologies needed to conduct a



feasibility study, viz.  receptor  macromolecule-complex recovery,  determination of receptor



binding kinetics, and immunoassays have developed sufficiently to be well documented in the



literature. Relatively minor modifications would be required for their application to a specific



biomarker.  Finally,  immunoassays  can be incorporated into biosensor devices which can



measure the amount of analyte in the blood in real time, i.e., at the time of sample acquisition.



Should feasibility be demonstrated, method  standardization, protocol  development,  method



comparison studies, QA/QC procedures, etc., would follow.
                                          31

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       Ten specific tasks are recommended in order to evaluate receptor-xenobiotic complex



concentration in the blood as a biomarker of human  exposure.  The  approximate order of



optimal undertaking is reflected in the following sequence:







1.      Verify the occurrence of AhR and GABAR in experimental animal and human blood



       cells using radiolabeled ligands with high specific binding, e.g., [3H]TCDD for AhR and



       [35S]TBPS for GABAR.



2.      For each  receptor,  determine the total  binding capacity (Bmax),  association  and



       dissociation rate constants (1^ and kj), apparent equilibrium dissociation constant (Kd),



       and stability  of the  receptor-xenobiotic  complex within the  sample in  vitro.   A



       considerable information base is already in existence for TCDD, making it the logical



       choice for the AhR.  Of the insecticidal compounds bound by the GABAR, endrin is



       preferred because of its high affinity constant.



3.      If blood cell GABA receptor concentrations are extremely low, the development of an



       immunoassay for one of the known pesticide ligands may not be practical. Accordingly,



       an alternative approach should be investigated concurrently with  steps 2-5.  Specifically,



       brain GABAR  should be used to bind the pesticide of interest in a plasma sample



       followed by isolation of the complex and quantitation using an immunoassay procedure.







4.      Obtain potyclonal antibodies for each receptor complex.   Develop and evaluate an



       immunoassay for each complex.  The specificity and/or sensitivity may be improved



       with the use of monoclonal antibodies if necessary.
                                          32

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5.      Using the immunoassay procedure developed, identify the useful dose-response range
       by  determining  the  concentration  of complex formed  at  different  xenobiotic
       concentrations in vitro.
6.      Plan and conduct a controlled study using experimental animals to verify the methods
       and  determine the relationship  between  exposure  and receptor-bound xenobiotic
       concentration.
7.      Initiate  the development of  a biosensor system  which  will transduce a quantitative
       chemical/physico-chemical reaction in the immunoassay system developed above into
       an electrical or optico-electrical signal which can be quantitatively processed.
8.      When feasible, identify a human population with known exposure to one or both of the
       above chemicals and  for which an epidemiological study is ongoing.   Compare the
       concentration of receptor-bound pesticide in the blood with other measures of exposure
       such as total blood concentration, urinary metabolite concentration, etc.
9.      A concurrent study should be carried on in conjunction with number one above.  This
       would involve selecting four or five additional high priority pesticides to determine
       whether these chemicals show specific binding to blood cell membrane preparations in
       vitro. Small groups of xenobiotics, examined periodically as time permits, provide a
       reservoir of potential biomarkers to be developed as funds and need permit.
10.    Three-dimensional molecular modeling software  should be used to study the potential
       for binding  of pesticides to  specific receptors  prior to  initiating  laboratory animal
       experiments.  These programs permit quantitative  information to be gained about
                                           33

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goodness  of fit between  a particular pesticide structure and  the receptor  based on



comparisons with ligands with known structures and affinities.
                                     34

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                                LITERATURE CITED







1.      Lippmann,  M., and G.D.  Thurston.   1988.   Exposure assessment:   input into risk



       assessment. Arch. Environ. Health 43(2): 113-123.







2.      Committee on Biological Markers of the National Research Council. 1987. Biological



       markers in environmental health research. Environ. Health Perspect. 74:3-9.







3.      Van Emon, J., J. Seiber, and B. Hammock.  1987. Application of an enzyme-linked



       immunosorbent assay  (ELJSA) to determine paraquat residues in  milk, beef,  and



       potatoes. Bull. Environ. Contam. Toxicol. 39:490-497.







4.      Triggle, D.J. 1980. Receptor-hormone interrelationships.  In Membrane Structure and



       Function, Vol. Three, E. Edward Bittar (ed.), John Wiley & Sons, p. 6.







5.      Sairam, M.R.   1985.  Protein gtycosylation and receptor-ligand interaction.  In: The



       Receptors, Vol. n, P.M. Conn (ed.), Academic Press, Inc., pp. 307-340.







6.      Limbird, Lee  E.   1986.   Cell Surface Receptors: A Short Course on  Theory and



       Methods. Martinus Nijhoff Publishing, Boston.
                                          35

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7.      Poland, A., and J.C. Knutson.  1982. 2,3,7,8-Tetrachlorodibenzo:p-dioxin and related



       halogenated aromatic hydrocarbons: Examination of the mechanism of toxicity.  Ann.



       Rev. Pharmacol. Toxicol. 22:517-554.







8.      Lowell,  J.L.,  and John E.  Casida.  1984.   Interactions of lindane,  toxaphene and



       cyclodienes with brain-specific  t-Butylbicyclo-phosphorothionate receptor.    Life



       Sciences 35:171-178.







9.      Hathaway,  D.E.   1984.  Molecular Aspects  of Toxicology.  The Royal Society  of



       Chemistry, London, pp. 277-291.







10.     Conn, P.M., ed. 1984.  The Receptors, Vol. I, Academic Press, Inc.







11.     Conn, P.M., ed. 1985.  The Receptors, VoL n, Academic Press, Inc.







12.     Conn, P.M., ed. 1986.  The Receptors, Vol. m, Academic Press, Inc.







13.     Conn, P.M., ed 1986.  The Receptors, Vol. IV, Academic Press, Inc.







14.     Wallach, Donald F.H.   1987.  Fundamentals of Receptor Molecule Biology. Mercel



       Decker, Inc.
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15.     Scatchard, G.   1949.  The attractions of Proteins for small molecules and ions. Ann.



       N.Y. Acad. Sci. 51:600-672.








16.     Rosenthal, H.E.  1967.  A graphic method for the determination and presentation of



       binding parameters in complex systems. Anal. Biochem. 20:525-532.








17.     Poland, A., E. Glover, and A.S. Kende.  1976.  Stereospecific, high-affinity binding of



       2,3,7,8-Tetrachlorodibenzo-p-dioxin  by hepatic cytosol:   evidence  that  the  binding



       species is receptor for  induction of aryl  hydrocarbon hydroxylase.   J.  Biol. Chem.



       251:4936-4946.








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