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*  t\  v        UNITED STATES ENVIRONMENTAL PROTECTION AGENCY
*                             WASHINGTON, D.C. 20460
                                  AugUSt 11, 1993               OFFICE OF THE ADMINISTRATOR
                                                                  SCIENCE ADVISORY BOARD
   EPA-SAB-EPEC-LTR-93-012
   Honorable Carol M, Browner
   Administrator
   U.S. Environmental Protection Agency
   401 M Street, S.W.
   Washington, DC  20460

         Subject:     Review of the Research Program for Environmental Release of
                     Biotechnology Products

   Dear Ms, Browner:

         The Biotechnology Research Review Subcommittee  of the Science Advisory ,
   Board's (SAB) Ecological Processes and Effects Committee met on February 18-19,
   1993, at the Gulf Breeze Environmental Research Laboratory to review the
   Agency's biotechnology research  program.  The Subcommittee reviewed the draft
   "Environmental Release of Biotechnology Products Research Plan" (dated May 29,
   1992} and other supporting documentation.

         We were asked by the Agency to evaluate both the ongoing research and the
   proposed future direction for the biotechnology research program.  Specifically, we
   were asked to assess the program's scientific productivity, use of extramural
   research, level of  interaction with other biotechnology research programs, proposed
   research  on transgenic'plants with pesticidal activity, and whether the research
   questions and approaches were appropriate and reflected the state of the  science.
   At the time of the review the Agency's biotechnology research effort was  in a
   period of transition to the draft  "Environmental Release of Biotechnology Products
   Research Plan." This 5-year research  plan was the primary focus of our review,
   although we also  addressed the productivity and results of previous research
   efforts.  We were  pleased to note that the  revised plan  incorporates several new
   elements and directions recommended by a previous SAB  review panel in 1988.

         Previous work by the Biotechnology Risk Assessment Research Program has
   made significant contributions to the scientific basis for assessing the potential
   risks associated with the development and release of biotechnology products. The
   early focus of the  Agency's  research program was on the development of methods
   and protocols for  determining the environmental  fate of released geneticaily-

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engineered microorganisms (OEMs).  The revised research plan proposes to apply
those protocols to assess potential risks associated with the deliberate or accidental
release of genetically modified organisms and pest control agents. We are
impressed by both the amount and quality of the Agency's research in this area,
and generally agree that the knowledge base is sufficient to allow this change in
program emphasis.

      The new research plan is the result of considerable work by individuals
from several Agency laboratories.  This planning group has done an excellent job
of defining the major issues surrounding the release of genetically modified
organisms into the environment, and has  formulated a comprehensive research
plan to  address these issues, We encourage the Agency to implement the plan,
with the modifications suggested below.  However, the plan is very ambitious, and
we question whether all aspects defined as important can realistically be addressed
given the personnel and funding likely to be available.  While the plan does
contain a list of seven priority research issues, there is little indication of priorities
among the specific projects within each research, area.  For example, there is no
indication of how implementation of the plan would be affected by changing
budgets (either increases or decreases),  The definition of critical information
needs should be done by the Office of Research and Development (QRD), in
cooperation with the Office of Prevention, Pesticides and Toxic Substances
(OPPTS).

      Our specific comments on each of the seven issue areas identified in the
plan will be addressed below.  However, we would first like to make some  general
observations on the program as a whole:

      a)    Much of the work to date has focused on  developing bioassays to
            measure the impact of GEMs on selected ecological endpoints. While
            this research has produced useful techniques and protocols, the
            results have shown that  impacts are difficult to  detect.   We suggest
            that future research place greater emphasis on:  1) identifying new,
            more sensitive, ecological endpoints for effects, and 2) understanding
            the fate of specific introduced organisms or genes,

      b)    The research program on release of biotechnology products should
            take full advantage of relevant  non-GEM models for assessing health
            effects, as well  as environmental fate and  effects where appropriate.
            The focus of the current biotechnology research program has been
            almost exclusively on the fate and effects of GEMs.  At the beginning
            of this effort that focus may have been appropriate. However, past
            work has shown little reason to believe that the fate and effects of
            GEMs are significantly different from that of other introduced
            microorganisms, such as those used for bioremediation.

      c)    Biotechnology products are a rapidly expanding field of endeavor with
            significant research being conducted by industry, academia, and other

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            government laboratories.  In light of the limited budget for research
            on fate and effects of these products, it  is  critical that the Agency
            take advantage of the information and resources that are available
            from other sources, While the biotechnology research group is in
            contact with several other government agencies, this interaction has
            been mostly in the form of sharing information about program goals
            and objectives.  We commend the ORD headquarters and laboratory
            personnel for the outreach efforts to date, but  we encourage greater
            attention to substantive interaction and  coordination with relevant
            groups.  For example, there are significant opportunities for sharing
            data, joint planning of research projects, and even collaborative
            studies, with agencies like the U.S. Department of Agriculture
            (USDA), Department of Energy (DOE), National Institutes of
            Environmental Health Sciences  (N1EHS) and the  Food and Drug
            Administration (FDA). In addition, the  Agency should  seek
            opportunities to expand collaboration with industry researchers,

COMMENTS ON SPECIFIC ISSUE AREAS

1.    BIOASSAY TECHNIQUES

      We support the objectives of the bioassay technique research area, as
described in the issue plan;  namely the development of test systems to detect
ecological effects. However, the research approach does not reflect this focus,
Greater emphasis should be placed on determining sensitive environmental
processes or endpoints where effects would be expected ("vulnerability
assessment"), and then developing bioassays for these sensitive points.
Researchers should not be constrained to using OEMs,  since the best system to
measure perturbations may be non-GEMs. In addition, this research need not be
directed totally to providing protocols for the Agency's regulatory programs.  The
microcosm research should support bioassay and gene survival research elements
as outlined in the research plan.

      We feel that further refinement of existing bioassays, which have not shown
significant effects, will not appreciably improve the Agency's ability to do risk
assessment of releases of OEMs or other biotechnology products. Greater
emphasis on identifying new ecologically relevant endpoints would be a more
productive research area.  The Agency has had the tendency to deal with
microorganisms as if they were chemicals,  with specific, constant properties and
environmental effects.  Microorganisms may be both more specific, in that their
effects may be much narrower than a single chemical, and more diverse, in that
they can catalyze many reactions.  Therefore, the research group should consider
broadening the  emphasis from single species  to consortia  or communities, which
are more realistic models of nature. Of course, exposure  should be related to
expected application methods, dosage, and  bioassay organism life stages at the
time of release.

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2,    GENE SURVIVAL

      The study of transfer of natural genetic elements under environmental
conditions is an important research area which should improve otir understanding
of the ecological significance of naturally-occurring gene transfer. However,
further development of sensitive (and sophisticated) tools to study the transfer of
DNA from GEMs could have limited utility from a risk assessment perspective.
Past and ongoing research by this team and others has demonstrated extremely
limited transfer of DNA between microorganisms under realistic, natural
conditions.   Further and more complex analysis of this low probability transfer is
unlikely to alter the risk evaluation based on DNA exchange.  In other words, if
we already have the ability to detect gene transfer at. ecologically relevant levels,
does development of the ability to  detect even lower levels add anything to our
ability to assess risk?

      In contrast,  the transfer of modified DNA from transgenic plants by pollen
or other mechanisms is not well  characterized, and therefore research in these
areas could improve the Agency's risk evaluations. We also encourage the Agency
to continue work on the mathematical modeling of gene transfer. Although
detectable transfer has been found in aqueous systems, microbial gene transfer
appears to be rare in soil environments, and modeling may be  the most reasonable
way  to assess the probability of gene transfer and the potential effects.  Such
modeling will provide focus and direction for micro-/mesocosm  research.

3.    MICRO-/MESOCOSMS

      The Agency has  a long and distinguished history of microcosm research and
has appropriately adapted that technology to biotechnology product fate studies,
The  goals of this research area have been largely completed since adequate micro-
/mesoeosm protocols now exist for  most current test systems. Remaining needs
may be the development of systems (including micro-/mesocosms with multiple
trophic levels) to complement newly developed bioassays, gene survival studies, or
ecological endpoints.

      The micrO'/misocosm research would benefit from a broader view toward
biological risk assessment  (microbes are not chemicals) and not being constrained
by working only with GEMs.  As noted previously, risk assessment is complicated
by the difficulty in defining measurable endpoints  for studying effects. Therefore,
we recommend that test systems be sought where  ecological effects can be
measured,

4.    TRANSGENIC PLANTS

      The proposed research on  transgenic plants, a new research area for the
Agency, is comprehensive in its scope and goals.  The  subject of transgenic plants,
particularly pesticidal plants,  is important because of the potential economic
significance of this new technology (several transgenic crop plants are close to

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commercialization), and the potential effects of food crops containing foreign genes
which produce insect toxins. The proposed research goals include a comprehensive
assessment of potential impacts on  soil organisms (bacteria and invertebrates)
from release of genetically engineered plants.  The research plan does aoj address
the possible human health risks from consumption of transgenic food crops or
toxic effects of pestieidal plants on  indigenous plants and animals.  These topics
should be addressed.  It is unlikely that the proposed research can be
accomplished with the levels of funding, resources, and staffing that are proposed
and likely to be realized in the near future. This suggests the need for greater
focus, and especially cooperation with other agencies.

      In order  to validate the protocols being developed  and ensure credibility for
this new research area, rigorous external peer review and use of extramural
funding is critical until the Agency  is able to strengthen  its in-house expertise in
plant ecology and plant molecular biology,  Because other agencies currently have
significant expertise in plant science, food science, etc., we recommend close liaison
with agencies such as the 0SDA and FDA.  These interagency interactions should
be directed toward true exchange of expertise, joint research planning, and joint
research projects in appropriate cases.

5,     RISK CONTROL FOR LARGE SCALE RELEASES

      We recommend that current  large scale release of non-indigenous organisms'
(non-GEMs) be used as a model system to evaluate potential effects  of large scale
releases of GEMs,   Land application of sludge, bioaugmentation projects and some
bioretnediation  projects all offer potential research sites.  Research on the effects
of releasing non-GEMs should also  be an important reference point for assessing
potential non-target impacts from a large scale GEM release. As already noted,
we encourage the Agency to develop and test fate methods and models because of
the difficulty in choosing appropriate  and sensitive endpoints for ecological effects.

      While much good science has been achieved under  the biological
containment project area, we question the use of this approach for large scale
commercial applications for two reasons.  First, introduction of lethal genes is
unlikely to be effective as a containment strategy.  When induced, the gene would
have to be lethal 100 percent of the time, and when not induced," produce  zero
gene product.  Since this scenario of perfect regulation is unlikely, natural
selection will almost certainly overcome any introduced lethal trait with the
development of resistance, Second,  the risk associated with introducing lethal
genes into the environment may exceed risks from the organisms to  be controlled.
Clearly, other mechanisms of control need to be  examined.

6,     HUMAN HEALTH EFFECTS

      The Agency's research on human health effects has been particularly
productive and  responsive to previous recommendations of the SAB and the needs
of the Agency.  The goals outlined in the research plan are reasonable, and the

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research questions are particularly relevant to a government agency.  However, we
believe that little is unique about the biological properties of GEMs which would
require  their exclusive use in this research effort.  Much is known about the
mfectivity of non-GEMs which is directly applicable to the health risk assessment
for GEMs,  The focus of research under this project area should be on
biotechnology products in general.

      We question the value of a new evaluation of toxic intermediates from
bioremediatlon, as proposed in this section of the plan,  NIEHS already has such
an evaluation as a major research goal, and duplication of this effort is
unnecessary. Also, the SAB's Environmental Engineering Committee, in its 1992
review of the Agency's bioremediation program, concluded that this research was
not high priority (SAB Report No. EPA-SAB-B1C-92-026),  If this work is pursued
by the Agency,  it should  only be in cooperation and coordination with NIEHS.

7.    LARGE-SCALE MANUFACTURING FACILITIES

      Most fermentation processes using GEMs presently follow cautionary
guidelines, such as Good Manufacturing Practices or the NIH/FDA guidelines for
large scale containment of microorganisms. The research plan does not  adequately
justify the need for more defined or stricter controls.  The proposed research
would benefit from greater input and interaction with potential users (the
fermentation industry), other relevant agencies (National Institute for Occupational
Safety and Health, and FDA), and industrial associations (e.g., Chemical
Manufacturers Association, and Pharmaceutical Manufacturers Association).
Information on engineering risk  control technologies may be more readily available
by transfer of existing data or technology from other organizations or equipment
manufacturers.

      In summary, we find that the Agency's research program on Environmental
Release of Biotechnology Products has been extremely productive and is  admirably
addressing both the science associated with environmental release of GEMs and
the Agency's need to assess risk.  For continued improvement, we urge the Agency
to consider the following recommendations:

      a)    establish priorities for research within the seven issue areas;

      b)    identify more sensitive ecological endpoints for effects;*

      c)    assess the fate of specific introduced organisms or genes;

      d)    utilize appropriate non-GEM models for assessing health and
            ecological effects;

      e)    increase coordination of research with other agencies and industry
            researchers; and,

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      f)     address possible human health and ecological effects of pestieidal
            plants.

      We are pleased to have had the opportunity to review the biotechnology
research  program. We hope our recommendations will assist the Agency to
strengthen and refine this important program, and we look forward to your
response.

                              Sincerely,
                              Dr, Raymond C, Loelir, Chair
                              Science Advisory Board
Dr. Kenneth L. Dickson, Chair
Ecological Processes and
1  Effects Committee
                                                                      jO*"****1*"*
Dr, Frederic K. PfaeiMJjIr, Chair
Biotechnology Research Review
  Subcommittee

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              U.S. ENVIRONMENTAL PROTECTION AGENCY
                       SCIENCE ADVISORY BOARD
         BIOTECHNOLOGY RESEARCH REVIEW SUBCOMMITTEE

                           February 18-19, 1993
CHAIR
      Dr. Frederic KL Pfamder, Institute for Environmental Studies, Department
      of Environmental Sciences and Engineering, University of North Carolina,
      Chapel Hill, North Carolina
MEMBERS/CONSULTANTS

      Dr. Burt D. Ensley, Emdrogen, Inc., Lawreneevile, New Jersey

      Dr. Daniel D. Jones, Federal Liaison, U.S. Dept. of Agriculture, Office of
      Agricultural Biotechnology, Washington, DC

      Dr. Philip J. Regal, Dept. of Ecology, Evolution & Behavior, University of
      Minnesota, St. Paul, Minnesota

      Dr. Donald W. Roberts, Insect Pathology Resource Center, Boyce Thompson
      Institute, Cornell University, Ithaca, New York

      Dr. James M. Tiedje, Center for Microbial Ecology, Michigan State
      University, East Lansing, Michigan


SCIENCE ADVISORY BOARD STAFF

      Stephanie Sanzone, Designated Federal Official, Science Advisory Board,
      U.S. EPA, 401 M Street, S,W, (A-101F), Washington, DC

      Marcia IL Jolly (Marcy), Staff Secretary, Ecological Processes and Effects
      Committee, Science Advisory Board, U.S. EPA, 401 M Street, S.W. (A-101F),
      Washington, DC

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                                   NOTICE

      This report has been written as a part of the activities of the Science
Advisory Board, a public advisory group providing extramural scientific
information and advice to the Administrator and other officials  of the
Environmental Protection Agency.  The Board is structured to provide balanced,
expert assessment of scientific matters related to problems facing the Agency.
This report has not been reviewed for approval by the Agency and, hence, the
contents of this report do not necessarily represent the views and policies of the
Environmental Protection Agency,  nor of other agencies in the Executive Branch
of the Federal government, nor does mention of trade names or commercial
products constitute a recommendation for use.

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